Cure SMA

Founded in 1984, Cure SMA leads the way to a world without spinal muscular atrophy, the number one genetic cause of death for infants. We fund and direct comprehensive research that drives breakthroughs in treatment and care, and we provide families the support they need for today. Our commitment to a treatment and cure is not just about seeking solutions—it's also about creating them. We're working with some of today's sharpest minds to advance a diversity of approaches and champion the most promising discoveries and methods.

http://curesma.org/